[Congressional Record Volume 171, Number 39 (Thursday, February 27, 2025)]
[Senate]
[Page S1433]
From the Congressional Record Online through the Government Publishing Office [www.gpo.gov]
SENATE RESOLUTION 104--DESIGNATING FEBRUARY 27, 2025, AS ``RARE DISEASE
DAY''
Mr. BARRASSO (for himself, Mr. Blumenthal, Ms. Klobuchar, Mr.
Marshall, Mr. Scott of South Carolina, Mr. Wicker, and Mr. Booker)
submitted the following resolution; which was considered and agreed to:
S. Res. 104
Whereas a rare disease or disorder is a disease or disorder
that affects a small number of patients;
Whereas, in the United States, a rare disease or disorder
is defined as affecting fewer than 200,000 individuals;
Whereas, as of the date of adoption of this resolution,
more than 30,000,000 individuals in the United States are
living with at least 1 of the more than 10,000 known rare
diseases or disorders;
Whereas children with rare diseases or disorders account
for a significant portion of the population affected by rare
diseases or disorders in the United States;
Whereas many rare diseases and disorders are serious and
life-threatening;
Whereas 2025 marks the 42nd anniversary of the enactment of
the Orphan Drug Act (Public Law 97-414; 96 Stat. 2049), a
landmark law enabling tremendous advances in the research and
treatment of rare diseases and disorders;
Whereas programs such as the Accelerating Rare disease
Cures Program of the Food and Drug Administration (referred
to in this preamble as the ``FDA'') aim to drive scientific
and regulatory innovation and engagement to accelerate the
availability of treatments for patients with rare diseases;
Whereas 26 of the 50 novel drugs approved by the Center for
Drug Evaluation and Research of the FDA in 2024--
(1) were approved to prevent, diagnose, or treat a rare
disease or condition; and
(2) received an orphan-drug designation;
Whereas, although the FDA has approved more than 882 drugs
and biological products with 1,300 orphan indications as of
the date of adoption of this resolution, approximately 95
percent of rare diseases still do not have a treatment
approved by the FDA for their condition;
Whereas financing life-altering and lifesaving treatments
can be challenging for individuals with a rare disease or
disorder and their families;
Whereas individuals with rare diseases or disorders can
experience difficulty in obtaining accurate diagnoses and
finding physicians or treatment centers with expertise in
their rare disease or disorder;
Whereas the National Institutes of Health support
innovative research on the treatment of rare diseases and
disorders;
Whereas Rare Disease Day is observed each year on the last
day of February; and
Whereas Rare Disease Day is a global event that was first
observed in the United States on February 28, 2009: Now,
therefore, be it
Resolved, That the Senate--
(1) designates February 27, 2025, as ``Rare Disease Day'';
and
(2) recognizes the importance of, with respect to rare
diseases and disorders--
(A) improving awareness;
(B) encouraging accurate and early diagnosis; and
(C) supporting national and global research efforts to
develop effective treatments, diagnostics, and cures.
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